Adenine base editing to mimic or correct disease mutations in rodents
1. Advanced Innovation Center for Human Brain Protection, National Clinical Research Center for Geriatric Disorders, Xuanwu Hospital of Capital Medical University, Beijing 100053, China
2. National Laboratory of Biomacromolecules, CAS Center for Excellence in Biomacromolecules, Institute of Biophysics, Chinese Academy of Sciences, Beijing 100101, China
3. University of Chinese Academy of Sciences, Beijing 100049, China
4. Gene Expression Laboratory, Salk Institute for Biological Studies, 10010 North Torrey Pines Road, La Jolla, California 92037, USA
5. Institute of Stem cell and Regeneration, Chinese Academy of Sciences, Beijing 100101, China
belmonte@salk.edu (J. C. I. Belmonte)
ghliu@ibp.ac.cn (G.-H. Liu)
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