CRISPR-based prime editing improves therapeutic outcomes for childhood alternating hemiplegia

Acknowledgements

This research was funded by the National Natural Science Foundation of China (grant Nos. 32470022 and 82020108021), Chongqing Outstanding Youth Funds (grant No. CSTB2025NSCQ-JQX), the National Natural Science Foundation of Chongqing (grant No. cstc2024ycjh-bgzxm0076), and the Fundamental Research Funds for the Central Universities (grant No. SWU-KR22013). Figure 1 was created with BioRender under a licensed agreement.

Conflict of interest

The authors declare no conflict of interest.

Notes

Editor’s note: A commentary on “In vivo prime editing rescues alternating hemiplegia of childhood in mice”

References

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