Highly efficient base editing in human tripronuclear zygotes

Changyang Zhou , Meiling Zhang , Yu Wei , Yidi Sun , Yun Sun , Hong Pan , Ning Yao , Wanxia Zhong , Yixue Li , Weiping Li , Hui Yang , Zi-jiang Chen

Protein Cell ›› 2017, Vol. 8 ›› Issue (10) : 772 -775.

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Protein Cell ›› 2017, Vol. 8 ›› Issue (10) : 772 -775. DOI: 10.1007/s13238-017-0459-6
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Highly efficient base editing in human tripronuclear zygotes

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Changyang Zhou, Meiling Zhang, Yu Wei, Yidi Sun, Yun Sun, Hong Pan, Ning Yao, Wanxia Zhong, Yixue Li, Weiping Li, Hui Yang, Zi-jiang Chen. Highly efficient base editing in human tripronuclear zygotes. Protein Cell, 2017, 8(10): 772-775 DOI:10.1007/s13238-017-0459-6

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References

[1]

KangX, HeW, HuangY, YuQ, ChenY, GaoX, SunX, FanY(2016) Introducing precise genetic modifications into human 3PN embryos by CRISPR/Cas-mediated genome editing. J Assist Reprod Genet33:581–588

[2]

KimK, RyuSM, KimST, BaekG, KimD, LimK, ChungE, KimS, KimJS (2017a) Highly efficient RNA-guided base editing in mouse embryos. Nat Biotechnol35:435–437

[3]

KimYB, KomorAC, LevyJM, PackerMS, ZhaoKT, LiuDR (2017b) Increasing the genome-targeting scope and precision of base editing with engineered Cas9-cytidine deaminase fusions. Nat Biotechnol35:371–376

[4]

KomorAC, KimYB, PackerMS, ZurisJA, LiuDR (2016) Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage. Nature533:420–424

[5]

LiangP, SunH, SunY, ZhangX, XieX, ZhangJ, ZhangZ, ChenY, DingC, XiongY(2017) Effective gene editing by high-fidelity base editor 2 in mouse zygotes. Protein Cell8(8):601–611

[6]

LiangP, XuY, ZhangX, DingC, HuangR, ZhangZ, LvJ, XieX, ChenY, LiY (2015) CRISPR/Cas9-mediated gene editing in human tripronuclear zygotes. Protein Cell6:363–372

[7]

LongC, McAnallyJR, SheltonJM, MireaultAA, Bassel-DubyR, OlsonEN (2014) Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA. Science345:1184–1188

[8]

MaY, ZhangJ, YinW, ZhangZ, SongY, ChangX (2016) Targeted AID-mediated mutagenesis (TAM) enables efficient genomic diversification in mammalian cells. Nat Methods13:1029–1035

[9]

NishidaK, ArazoeT, YachieN, BannoS, KakimotoM, TabataM, MochizukiM, MiyabeA, ArakiM, HaraKY (2016) Targeted nucleotide editing using hybrid prokaryotic and vertebrate adaptive immune systems. Science 353:aaf8729

[10]

TangL, ZengY, DuH, GongM, PengJ, ZhangB, LeiM, ZhaoF, WangW, LiX (2017) CRISPR/Cas9-mediated gene editing in human zygotes using Cas9 protein. Mol Genet Genom292:525–533

[11]

WangH, YangH, ShivalilaCS, DawlatyMM, ChengAW, ZhangF, JaenischR (2013) One-step generation of mice carrying mutations in multiple genes by CRISPR/Cas-mediated genome engineering. Cell153:910–918

[12]

WuY, LiangD, WangY, BaiM, TangW, BaoS, YanZ, LiD, LiJ (2013) Correction of a genetic disease in mouse via use of CRISPR-Cas9. Cell Stem Cell13:659–662

[13]

YangH, WangH, ShivalilaCS, ChengAW, ShiL, JaenischR(2013) One-step generation of mice carrying reporter and conditional alleles by CRISPR/Cas-mediated genome engineering. Cell154:1370–1379

[14]

ZongY, WangY, LiC, ZhangR, ChenK, RanY, QiuJL, WangD, GaoC (2017) Precise base editing in rice, wheat and maize with a Cas9-cytidine deaminase fusion. Nat Biotechnol35:438–440

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