Making the impossible possible: Baby KJ and the road map to personalized gene-editing care

Vanessa Almendro , Sadik H. Kassim

Clinical and Translational Medicine ›› 2025, Vol. 15 ›› Issue (11) : e70515

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Clinical and Translational Medicine ›› 2025, Vol. 15 ›› Issue (11) : e70515 DOI: 10.1002/ctm2.70515
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Making the impossible possible: Baby KJ and the road map to personalized gene-editing care

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Vanessa Almendro, Sadik H. Kassim. Making the impossible possible: Baby KJ and the road map to personalized gene-editing care. Clinical and Translational Medicine, 2025, 15(11): e70515 DOI:10.1002/ctm2.70515

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Kenjo E, Hozumi H, Makita Y, et al. Low immunogenicity of LNP allows repeated administrations of CRISPR-Cas9 mRNA into skeletal muscle in mice. Nat Commun. 2021; 12(1): 7101

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Lauffer MC, van Roon-Mom W, Aartsma-Rus A, et al. Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders. Commun Med (Lond). 2024; 4(1): 6.

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2025 The Author(s). Clinical and Translational Medicine published by John Wiley & Sons Australia, Ltd on behalf of Shanghai Institute of Clinical Bioinformatics.

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